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UID:25b3f50ceb3539217560dbaa90d05120
CATEGORIES:3e Jeudi
SUMMARY:Gene therapy advances
LOCATION:IMAGINE Institut – Hôpital Necker-Enfants Malades, Paris
DESCRIPTION;ENCODING=QUOTED-PRINTABLE:<p style="text-align: center;"><strong>Gene therapy advances (Marina Cavazz
 ana)</strong></p><p>10:00 &ndash; 12:45<br />o Introduction Pr. Marina Cava
 zzana<br />o "Gene therapy of blood genetic disorders by lentiviral vector-
 mediated gene transfer to hematopoietic stem cells". Pr. Fulvio Mavilio<br 
 />o AAV-mediated gene therapy of inherited retinal diseases and mucopolysac
 charidosis VI&rdquo;. Pr Auricchio<br />o &ldquo;Genome editing approaches 
 for beta-hemoglobinopathies&rdquo;. Pr. Annarita Miccio,</p><p><strong>Aprè
 s-midi coordonnée par l&rsquo;Equipe de Génétique, HCL, CLAD Centre Est</st
 rong><br />o 14:00 &ndash; 14:30: Roifman Syndrome<br />o 14:30 &ndash; 14:
 45: « 15 minutes NGS »<br />o 14:45 &ndash; 16:00: Cas cliniques</p><p>Merc
 i d&rsquo;adresser les observations NGS et les cas cliniques à massimiliano
 .rossi01@chu-lyon.fr</p><p>16:00 &ndash; 18:30 : <strong>Assemblée Générale
  annuelle de la filière AnDDI-Rares (incluant une conférence de Mme A. Chev
 rier, PNMR3)</strong></p>
CONTACT:massimiliano.rossi01@chu-lyon.fr
DTSTAMP:20260410T073042Z
DTSTART;TZID=Europe/Paris;VALUE=DATE:20170615
DTEND;TZID=Europe/Paris;VALUE=DATE:20170616
SEQUENCE:0
TRANSP:OPAQUE
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